Posted on 23 September 2024
The critical evaluation was conducted by the Centre for Reviews and Dissemnation (CRD) and the Centre for Health Economics (CHE) Technology Assessment Group, leading to a positive recommendation for the first oral treatment for this rare blood disorder. CRD colleagues contributing to the appraisal were Mark Rodgers, Chinyereugo Umemneku-Chikere, Helen Fulbright, Alison Eastwood and Sofia Dias.
See our Technology Assessment Review programme of work to read about our evaluations for NICE over the last 25 years.